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Identification of on-target mutagenesis during correction of a beta-thalassemia splice mutation in iPS cells with optimised CRISPR/Cas9-double nickase reveals potential safety concerns

  • Suad Alateeq
  • , Dmitry Ovchinnikov
  • , Timothy Tracey
  • , Deanne Whitworth
  • , Abdullah Al-Rubaish
  • , Amein Al-Ali
  • , Ernst Wolvetang*
  • *Corresponding author for this work
  • University of Queensland
  • Imam Abdulrahman Bin Faisal University

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