Identification of on-target mutagenesis during correction of a beta-thalassemia splice mutation in iPS cells with optimised CRISPR/Cas9-double nickase reveals potential safety concerns
- Suad Alateeq
- , Dmitry Ovchinnikov
- , Timothy Tracey
- , Deanne Whitworth
- , Abdullah Al-Rubaish
- , Amein Al-Ali
- , Ernst Wolvetang*
*Corresponding author for this work
- University of Queensland
- Imam Abdulrahman Bin Faisal University
Research output: Contribution to journal › Article › peer-review
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